Scholar Rock is asking the U.S. Food and Drug Administration to approve apitegromab for people with spinal muscular atrophy.

Inclement weather can pose a threat to people like columnist Ari Anderson, who depend on in-home care. Such are the storms of ...

Icy paths and cold temperatures pose challenges for columnist Kevin Schaefer, a power wheelchair user who's living with SMA.

More research is needed to confirm gray matter, the darker tissue found in the brain and spinal cord, “as a potential disease ...

A woman with SMA type 3 became pregnant while on Spinraza treatment and gave birth to a healthy child, per a case report.

Regulators in the U.S. and the European Union agreed to review Biogen’s applications for approval of a higher dose Spinraza ...

Problems with chemical messengers like dopamine were tied to posture issues in SMA in a mouse study, but levodopa therapy may ease symptoms.

Columnist Helen Baldwin gains a different perspective following a crushing diagnosis, but glasses weren't what helped her to see clearly.

Blood levels of creatinine, a byproduct of normal muscle function, may be a potential biomarker of disease severity and treatment response in adults and adolescents with spinal muscular atrophy (SMA), ...

Nonadherence of spinal muscular atrophy (SMA) patients to their prescribed regimen of Evrysdi (risdiplam) — an oral solution generally taken once daily after a meal — is associated with higher ...