A case report described an infant with concurrent HDFN and SMA who was succesfully treated with an onasemnogene abeparvovec infusion.
Bristol Myers Squibb today announced the Committee for Medicinal Products for Human Use (CHMP) of the European Medicines Agency (EMA) has recommended approval of Breyanzi® (lisocabtagene maraleucel; ...
President Trump has appointed Chris Rocheleau as the acting FAA administrator following a tragic aircraft collision near Washington, D.C. Rocheleau, with over two decades of experience at the FAA ...